Genetic disorders occur due to alterations in the primary genetic material—deoxyribonucleic acid (DNA)—of an organism.
The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...
Our understanding of DNA has grown dramatically over the past couple of decades. The CRISPR technology, which allows scientists to map and even change DNA, has helped to boost that understanding even ...
CRISPR–Cas9-based therapies are widely investigated for their clinical applications. However, there are limitations ...
A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. The baby, KJ Muldoon of Clifton Heights, ...
Urnov is a professor of molecular therapeutics at the University of California, Berkeley, and a director at its Innovative Genomics Institute. In May, news broke of a biomedical first: the on-demand ...
Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...