Learn about Amyotrophic Lateral Sclerosis (ALS), its symptoms, risk factors, diagnosis, and current research advancements.

The FDA has approved Itvisma for the treatment of children two years and older, teens and adults living with spinal muscular ...

The experimental therapy M102 slowed disease progression in preclinical experiments done in mouse and cell models of ALS, a ...

Novartis wins FDA approval for Itvisma, a one-time gene therapy offering broader SMA treatment with sustained motor function ...

Euphoria star Eric Dane was diagnosed with amyotrophic lateral sclerosis, known as ALS in April 2025. Learn all about his ...

Itvisma contains the active ingredient in Zolgensma approved in 2019 for children younger than 2 years but is reformulated ...

Novartis secures FDA approval for Itvisma, a one-time gene therapy designed to boost motor function across a broad SMA ...

Onasemnogene abeparvovec-brve is the first gene replacement therapy approved for SMA patients aged 2 years and older, expanding access beyond infants. Phase 3 trials demonstrated significant motor ...

FDA cleared Itvisma as the first gene-replacement therapy available to people 2 and older with the rare muscle-weakening ...

Quickly approved by national drug authority Anvisa under priority review, the study positions Brazil at the forefront of the field in Latin America.

A paralyzed man has become the first person to operate an iPad using only his thoughts. The breakthrough arrived through a ...

A new DoD-funded trial tests SwallowFIT, a targeted therapy that strengthens swallowing muscles in early Parkinson’s patients ...