Novartis receives FDA approval for Itvisma(R), the only gene replacement therapy for children two years and older, teens, and adults with spinal muscular atrophy (SMA)

ITVISMA is a prescription gene therapy used to treat adults and children 2 years of age and older with spinal muscular atrophy (SMA). ITVISMA is given as a one-time intrathecal injection. What is the ...
Le Lézard

Novartis receives FDA approval for Itvisma®, the only gene replacement therapy for children two years and older, teens, and adults with spinal muscular atrophy (SMA)

Novartis today announced that the US Food and Drug Administration (FDA) has approved Itvisma® (onasemnogene?abeparvovec-brve) for the treatment of children two years and older, teens, and adults ...
Mid-Day

How former RJ Sapna Rana, living with incurable ALS, is documenting her difficult journey

ALS is a deadly disease that has no known cause, and no cure. But former RJ Sapna, who has been documenting her ...
The Times Leader

‘It works, it really works’: Kingston woman part of clinical drug trial

In 2021, Stacye Westington tripped over a rug, and as she lay on the floor in her Kingston home, she became aware that a glass she had been holding was broken. A shard was cutting her arm. It hurt.
Mid-Day on MSN

How Sapna Rana, living with incurable ALS, is documenting her difficult journey

There`s an entire generation that has grown up listening to Sapna Rana’s voice on the radio. Remember the tagline “It’s hot” ...
Outlookindia

Your Tongue Could Reveal Early Signs Of Motor Neurone Disease, Researchers Discover

Scanning MRI of a person's tongue may help in the early detection and ongoing monitoring of Motor Neurone Disease (MND), a neurodegenerative disease, according to a study. The researchers from the ...
Midland Daily News on MSN

Savvy Senior: What are the early signs of Parkinson’s Disease?

Recognizing the early signs of Parkinson’s disease is challenging because the symptoms are often subtle and/or similar to ...

Stuart Broad's life with 'split' from Mollie King and heartbreak that was kept secret

England cricket legend Stuart Broad's personal life has been marked by romance, heartbreak and business ventures beyond the ...
Manchester Evening News

New drug could 'slow progression' of motor neurone disease and offer 'real hope'

Scientists have discovered a new drug that offers "real hope" in the treatment of motor neurone disease (MND). The medicine, named M102 works by protecting nerve cells damaged by the disease. Studies ...
The Mirror

New drug breakthrough could slow progression of 'one of the cruellest diseases'

Scientists have discovered a new drug that protects nerve cells damaged by 'one of the cruellest diseases', offering hope of significantly slowing its progression. Early-stage research involving M102 ...
The Mirror

Rugby star Lewis Moody shares family update after heartbreaking MND diagnosis

Former rugby union player Lewis Moody has opened up about how his family are coping with his Motor Neurone Disease (MND) diagnosis after revealing the devastating news last month. The 47-year-old ...
The Independent

Rob Burrow’s family opens MND centre in honour of late rugby league star

From reproductive rights to climate change to Big Tech, The Independent is on the ground when the story is developing. Whether it's investigating the financials of Elon Musk's pro-Trump PAC or ...