Alcohol addiction devastates millions of lives each year, tearing apart families and leaving lasting scars. Yet, amid the ...

In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...

Looking forward, greater use of column chromatography technologies in vector manufacturing could facilitate the adoption of ...

CRISPR is like an editor that can rewrite DNA letter by letter or gene by gene, to remove harmful mutations or add protective ...

PRGN-2012—which Precigen has begun to call by its generic name of zopapogene imadenovec—is a gene therapy designed to elicit immune responses directed against cells infected with human papillomavirus ...

A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...

Retinal gene therapy advancements may rewrite the book on treatments for age-related macular degeneration and diabetic eye diseases.

As FDA seeks to rehire some fired employees, Donald Trump threatens to enact tariffs on pharma companies unless they reshore manufacturing; another lawsuit hits the complex GLP-1 compounding space as ...

Early results from the company’s single-arm trial saw the therapy able to partially repair the chemical responsible for ...

New research reveals that voluntary exercise restores STAT3 levels in the amygdala, helping to prevent stress-induced ...

Qure's stock rises on Huntington's therapy progress and strong gene therapy pipeline. Learn about QURE stock's cost-cutting ...

Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...