The FDA has approved Itvisma for the treatment of children two years and older, teens and adults living with spinal muscular ...

Parkinson's disease (PD) is an age-related, progressive neurodegenerative disorder. The hallmark of PD pathogenesis is the ...

Itvisma contains the active ingredient in Zolgensma approved in 2019 for children younger than 2 years but is reformulated ...

Onasemnogene abeparvovec-brve is the first gene replacement therapy approved for SMA patients aged 2 years and older, expanding access beyond infants. Phase 3 trials demonstrated significant motor ...

Novartis wins FDA approval for Itvisma, a one-time gene therapy offering broader SMA treatment with sustained motor function ...

Researchers in Australia have identified a three-drug combination that greatly extends the survival of motor neuron cells in ...

ITVISMA is a prescription gene therapy used to treat adults and children 2 years of age and older with spinal muscular atrophy (SMA). ITVISMA is given as a one-time intrathecal injection. What is the ...

A 19-year-old who was diagnosed with a rare form of motor neurone disease (MND) in August has said it is "disgusting" that ...

Sinfield revealed this year's ultramarathon challenge - taking in more than 50km (31 miles) each day - would take place in ...

The experimental therapy M102 slowed disease progression in preclinical experiments done in mouse and cell models of ALS, a ...

The Prince of Wales met Burrow’s children, his wife Lindsey, and his rugby team-mate Kevin Sinfield when he opened the new MND centre in Leeds.

On Thursday, Nov. 20, Prince William headed to Leeds in the north of England for an emotional reunion with the widow of rugby ...